Gene Therapy Trial Data Suggests Efficacy in the Presence of Antibodies
The recent American Society of Gene & Cell Therapy (ASGCT) Virtual Meeting featured updates from the phase III HOPE-B clinical trial of etranacogene dezaparvovec, an investigational gene therapy...
View ArticleBioMarin Presents Positive Safety and Efficacy Data for their Hemophilia A...
BioMarin recently reported key findings from preclinical studies of their investigational, gene therapy Roctavian (valoctocogene roxaparvovec), which was developed for the treatment of adults with...
View ArticleNew Affordable Care Act Ruling Benefits Chronic Disease Patients
FOR IMMEDIATE RELEASEMedia Contact Ilana Ostriniostrin@hemophilia.org 212-328-3769
View ArticleNew Article Offers Scientific Overview of AAV Vectors and Hemophilia Gene...
A new article, “Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for Hemophilia,” was published in the Journal of Clinical Medicine (JCM).
View ArticleNew Paper Explores Shared Decision Making in Hemophilia
A new paper published in The Journal of Haemophilia Practice advances the concept of shared decision making (SDM) between the hemophilia patient and their healthcare provider (HCP).
View ArticleLearn More About Shared Decision Making in Hemophilia
Shared decision making (SDM), the concept by which patients and healthcare providers work closely together to arrive at personalized treatment-related decisions, can have significant positive impacts...
View ArticleCo-pay Accumulator Policies Hurt Patients. There’s a Simple Solution.
This piece is a joint effort by Amy Niles, executive vice president at the PAN Foundation, and Kollet Koulianos, vice president of payer relations at the National Hemophilia Foundation. Each year on...
View ArticleNew Medscape Activity Seeks to Prepare Clinicians for Gene Therapy
Medscape has launched a new enduring activity designed to enhance clinicians’ awareness of gene therapy for hemophilia and increase their confidence when it comes to the eventual integration of these...
View ArticleTakeda Announces Approval of Prophylactic Indication for VWD Therapy
Takeda recently announced that the U.S. Food and Drug Administration (FDA) has approved VONVENDI® for routine prophylaxis to reduce the frequency of bleeding episodes in adults with severe Type 3 von...
View ArticleUpdate from BioMarin Phase 3 trial
Please click this link to read an update from BioMarin on a phase 3 trial.
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Meet MASAC’s New Chair: Dr. Amy Dunn
One patient changed Dr. Amy Dunn’s entire career the first-year of residency. It was then that Dr. Dunn diagnosed her first patient with hemophilia.
View ArticlePublic Health for Blood Disorders Series Now Available Online!
In 2020 NHF began an exciting collaboration with a number of blood disorder groups who receive funding from the Centers of Disease Control and Prevention.
View ArticleNHF Statement: Russian Attack on Ukraine
As the eyes of the world fix upon Ukraine, I am shocked and saddened to see heartbreaking images emerge showing injured civilians staggering through the streets and towns in the east of the country...
View ArticleStarting the Conversation with Dr. Johnny Mahlangu
Dr. Johnny Mahlangu gracious sat down with NHF's CEO Dr. Len Valentino for an informative dialogue to honor Black History Month and World Hemophilia Day. Read these Q&As and watch the video to...
View ArticleNational Hemophilia Foundation “Starts the Conversation” During Bleeding...
Awareness month campaign encourages the community to raise their voices and share what is most important and relevant to their conditions throughout March.FOR IMMEDIATE RELEASEMEDIA CONTACT:Ilana...
View ArticleHANDI Team Reminder – Apply for 2022 Scholarships Now!
It’s almost that time of year!Each year, HANDI compiles an annual list of post-secondary educational scholarships that are available to students living with inheritable bleeding disorders and their...
View ArticleStarting the Conversation with Dr. Marybec Griffin
Dr. Marybec Griffin graciously sat down with NHF for an informative dialogue to share information on her co-authored Twitter account, Dr. Period Hackers.
View ArticleStarting the Conversation with Dr. Bethany Samuelson Bannow
Dr. Bethany Samuelson Bannow sat down with NHF to discuss her co-authored Twitter account, Dr. Period Hackers. Read these Q&As and watch the video to learn more!What inspired you to start Dr....
View ArticleStarting the Conversation with Hajar Abusief
Student Hajar Abuisef sat down with NHF to discuss her involvement in the Twitter account, Dr. Period Hackers. Read these Q&As, and watch the video to learn more!How did you come to be a part of...
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